沙丙蝶呤
Sapropterin | (6R)-BH4 | (6R)-Tetrahydro-L-biopterin)
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Product Name Sapropterin | (6R)-BH4 | (6R)-Tetrahydro-L-biopterin)
CAS62989-33-7
FormulaC9H15N5O3
MW241.25
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Product details

Sapropterin ((6R)-BH4) is an orally active phenylalanine hydroxylase (PAH) cofactor, which is effective in reducing blood phenylalanine concentrations. Sapropterin can be used in study of phenylketonuria (PKU).


Related literature
PMID: 33844153 PMCID: PMC8609075 DOI: 10.1007/s13311-021-01043-4
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